35
Participants
Start Date
January 13, 2014
Primary Completion Date
October 2, 2017
Study Completion Date
October 2, 2017
BMN 111
BMN 111 will be administered daily for 24 months in an open-label sequential dose adjustment fashion.
Murdoch Children's Research Institute, Parkville
Johns Hopkins McKusick - Institute of Genetic Medicine, Baltimore
Ann and Robert H. Lurie Childrens Hospital of Chicago, Chicago
Institut Necker, Paris
Baylor College of Medicine, Houston
Harbor - UCLA Medical Center, Torrance
Children's Hospital & Research Center Oakland, Oakland
Vanderbilt University, Nashville
Guys & St. Thomas NHS Foundation Trust Evelina Hospital, London
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY