A Phase 2 Study of BMN 111 to Evaluate Safety, Tolerability, and Efficacy in Children With Achondroplasia

PHASE2CompletedINTERVENTIONAL
Enrollment

35

Participants

Timeline

Start Date

January 13, 2014

Primary Completion Date

October 2, 2017

Study Completion Date

October 2, 2017

Conditions
Achondroplasia
Interventions
DRUG

BMN 111

BMN 111 will be administered daily for 24 months in an open-label sequential dose adjustment fashion.

Trial Locations (9)

3052

Murdoch Children's Research Institute, Parkville

21287

Johns Hopkins McKusick - Institute of Genetic Medicine, Baltimore

60611

Ann and Robert H. Lurie Childrens Hospital of Chicago, Chicago

75015

Institut Necker, Paris

77030

Baylor College of Medicine, Houston

90509

Harbor - UCLA Medical Center, Torrance

94609

Children's Hospital & Research Center Oakland, Oakland

37232-2578

Vanderbilt University, Nashville

SE1 9RT

Guys & St. Thomas NHS Foundation Trust Evelina Hospital, London

Sponsors
All Listed Sponsors
lead

BioMarin Pharmaceutical

INDUSTRY