61
Participants
Start Date
March 31, 2014
Primary Completion Date
July 31, 2017
Study Completion Date
July 31, 2017
Treosulfan
Treosulfan will be administered over 3 days prior to HSCT at the following dose: 10 g/m2 (children aged \< 3months) or 12 g/m2 (children aged 3/12 months) or 14 g/m2 (children aged \> 12 months)
Great Ormond Street Hospital for Children, London
Great North Childrens Hospital, Newcastle upon Tyne
Newcastle-upon-Tyne Hospitals NHS Trust
OTHER
Great Ormond Street Hospital for Children NHS Foundation Trust
OTHER