Natural History Studies of Mucopolysaccharidosis III

CompletedOBSERVATIONAL
Enrollment

25

Participants

Timeline

Start Date

February 28, 2014

Primary Completion Date

November 30, 2015

Study Completion Date

November 30, 2015

Conditions
Mucopolysaccharidosis Type IIIAMucopolysaccharidosis Type IIIB
Interventions
PROCEDURE

Lumbar puncture

DEVICE

Magnetic Resonance Imaging (MRI) of the brain

Trial Locations (1)

43205

Nationwide Children's Hospital, Columbus

All Listed Sponsors
collaborator

Sanfilippo Children's Research Foundation

UNKNOWN

collaborator

The Sanfilippo Research Foundation

UNKNOWN

collaborator

The Children's Medical Research Foundation

UNKNOWN

lead

Nationwide Children's Hospital

OTHER

NCT02037880 - Natural History Studies of Mucopolysaccharidosis III | Biotech Hunter | Biotech Hunter