36
Participants
Start Date
February 28, 2014
Primary Completion Date
September 20, 2017
Study Completion Date
September 20, 2017
UX007
oral liquid
Placebo
oral liquid
Melbourne Brain Centre, Heidelberg
Columbia University - Department of Neurology, New York
Columbia University Medical Center, New York
Neurology & Epilepsy Research Center, Orlando
Miami Children's Research Institute, Miami
Service de Neurologie Pédiatrique et des Maladies Métaboliques - INSERM U1141 Hôpital Robert Debré - APHP, Paris
Cook Children's Hospital, Fort Worth
University of Texas Neurometabolic Clinic, Houston
Children's Hospital Colorado - University of Colorado, Denver, School of Medicine, Aurora
Seattle Children's Hospital, Seattle
Sheba University Medical Center, Tel Aviv
"Unita' Operativa Neurologia Pediatrica e Malattie Muscolari Istituto Giannina Gaslini", Genova
Hospital Sant Joan de Deu, Barcelona
Newcastle University, Newcastle upon Tyne
Ultragenyx Pharmaceutical Inc
INDUSTRY