BMN 110 Phase 3B in Australian Patients

PHASE3CompletedINTERVENTIONAL
Enrollment

13

Participants

Timeline

Start Date

July 31, 2013

Primary Completion Date

July 31, 2016

Study Completion Date

December 31, 2016

Conditions
Mucopolysaccharidosis IVA (Morquio A Syndrome)
Interventions
DRUG

BMN 110

All pateints receive treatment with BMN 110

Trial Locations (5)

2145

Children's Hospital at Westmead, Westmead

3052

Murdoch Childrens Research Institute and Royal Children's Hospital, Melbourne

6008

Princess Margaret Hospital for Children, Perth

4101 (4029)

Lady Cilento Children's Hospital (previous: Royal Children's Hospital), Brisbane

5OOO

Pain and Anaesthesia Research Clinic, Royal Adelaide Hospital, Adelaide

Sponsors
All Listed Sponsors
lead

BioMarin Pharmaceutical

INDUSTRY