Safety and Efficacy of Clenbuterol in Individuals With Late-onset Pompe Disease and Receiving Enzyme Replacement Therapy
PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment
17
Participants
Timeline
Start Date
September 30, 2013
Primary Completion Date
September 2, 2016
Study Completion Date
September 2, 2016
Conditions
Pompe Disease
Interventions
DRUG
Clenbuterol
DRUG
Placebo
Trial Locations (1)
27710
Duke University Medical Center, Durham
All Listed Sponsors
lead
Dwight Koeberl, M.D., Ph.D.
OTHER
NCT01942590 - Safety and Efficacy of Clenbuterol in Individuals With Late-onset Pompe Disease and Receiving Enzyme Replacement Therapy | Biotech Hunter | Biotech Hunter