8
Participants
Start Date
June 30, 2013
Primary Completion Date
September 30, 2022
Study Completion Date
September 30, 2022
Lamazym
ERT, i.v. infusions weekly
Center for Metabolic Diseases, Department of Clinical Genetics, Juliane Marie Centre, Copenhagen University Hospital, Blegdamsvej 9, Copenhagen
Chiesi Farmaceutici S.p.A.
INDUSTRY