Safety and Pharmacology Study of VP 20629 in Adults With Friedreich's Ataxia

PHASE1CompletedINTERVENTIONAL
Enrollment

46

Participants

Timeline

Start Date

August 13, 2013

Primary Completion Date

June 18, 2015

Study Completion Date

June 18, 2015

Conditions
Friedreich's Ataxia
Interventions
DRUG

VP 20629

DRUG

Placebo

Trial Locations (5)

19104

Children's Hospital of Philadelphia, Philadelphia

30329

Emory University, Atlanta

33612

University of South Florida, Tampa

52242

University of Iowa Children's Hospital, Iowa City

90095

UCLA Medical Center, Los Angeles

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Shire

INDUSTRY