100
Participants
Start Date
January 18, 2013
Primary Completion Date
October 5, 2016
Study Completion Date
October 5, 2016
University of North Carolina Division of Genetics and Metabolism, Chapel Hill
Hospital Infantil Universitario, Madrid
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Childrens Hospital & Research Center Oakland, Oakland
Hospital Universitario Austral, Pilar
Instituto Nacional De Pediatria, Mexico City
Central Manchester University Hospitals NHS Foundation Trust Willink Biochemical Genetics Unit, St. Mary's Hospital, Manchester
Lead Sponsor
Shire
INDUSTRY