NCT01801709View on ClinicalTrials.gov

Intracerebral Gene Therapy for Children With Early Onset Forms of Metachromatic Leukodystrophy

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

5

Participants

Timeline

Start Date

June 30, 2014

Primary Completion Date

June 30, 2016

Study Completion Date

December 20, 2022

Conditions
Metachromatic Leukodystrophy
Interventions
GENETIC

intracerebral administration of AAVrh.10cuARSA

Trial Locations (1)

Unknown

Bicêtre Hospital - Paris Sud, Le Kremlin-Bicêtre

All Listed Sponsors
collaborator

European Leukodystrophy Association

OTHER

collaborator

Assistance Publique - Hôpitaux de Paris

OTHER

lead

Institut National de la Santé Et de la Recherche Médicale, France

OTHER_GOV

NCT01801709 - Intracerebral Gene Therapy for Children With Early Onset Forms of Metachromatic Leukodystrophy | Biotech Hunter | Biotech Hunter