Acid Lipase Replacement Investigating Safety and Efficacy (ARISE) in Participants With Lysosomal Acid Lipase Deficiency

PHASE3CompletedINTERVENTIONAL
Enrollment

66

Participants

Timeline

Start Date

January 22, 2013

Primary Completion Date

May 30, 2014

Study Completion Date

December 11, 2018

Conditions
Lysosomal Acid Lipase Deficiency
Interventions
DRUG

Sebelipase Alfa

IV infusions of sebelipase alfa

DRUG

Placebo

IV infusions of matched placebo

Trial Locations (40)

10029

New York

11030

Manhasset

14222

Buffalo

19104

Philadelphia

19803

Wilmington

45229

Cincinnati

85724

Tucson

94304

Palo Alto

94143-0214

San Francisco

60611-2605

Chicago

02115

Boston

Unknown

Córdoba

Brisbane

New Lambton

Parkville

Perth

Zagreb

Olomouc

Prague

Paris

Vandœuvre-lès-Nancy

Freiburg im Breisgau

Mainz

Munich

Bergamo

Genoa

Padua

Tokyo

Tottori

Mexico City

Warsaw

Moscow

Elche

Madrid

Oviedo

Ankara

Izmir

Cambridge

London

Plymouth

Sponsors
All Listed Sponsors
lead

Alexion Pharmaceuticals, Inc.

INDUSTRY