269
Participants
Start Date
September 1, 2012
Primary Completion Date
October 1, 2016
Study Completion Date
October 1, 2016
Observational study
There is no medication or device tested in this study. This is an obversational study on the progression of the disease.
Nationwide Children's Hospital, Columbus
Cincinnati Children's Hospital Medical Center, Cincinnati
UC Davis Health System, Sacramento
Hospital de Pediatria Prof Dr Juan P Garrahan, Buenos Aires
Universitair Ziekenhuis, Ghent
Universitair Ziekenhuis Leuven, Leuven
Hospital das Clinicas da Faculdade de Medicina da USP, São Paulo
CHU Hopital des enfants, Toulouse
Universitaetsklinikum Essen, Essen
Universitaetsklinikum Freiburg, Freiburg im Breisgau
Azienda Ospedaliera Universitaria Policlinico G. Martino, Messina
Policlinico Univsersitario Agostino Gemelli, Rome
Leids Universitair Medisch Centrum, Leiden
UMC St. Radboud, Nijmegen
Drottning Silvias Barn- ochungdomssjukhus, Gothenburg
Hacettepe University Medical Faculty, Ankara
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY