A Prospective Natural History Study of Progression of Subjects With Duchenne Muscular Dystrophy.

TerminatedOBSERVATIONAL
Enrollment

269

Participants

Timeline

Start Date

September 1, 2012

Primary Completion Date

October 1, 2016

Study Completion Date

October 1, 2016

Conditions
Duchenne Muscular Dystrophy
Interventions
OTHER

Observational study

There is no medication or device tested in this study. This is an obversational study on the progression of the disease.

Trial Locations (16)

43205

Nationwide Children's Hospital, Columbus

45229

Cincinnati Children's Hospital Medical Center, Cincinnati

95817

UC Davis Health System, Sacramento

Unknown

Hospital de Pediatria Prof Dr Juan P Garrahan, Buenos Aires

Universitair Ziekenhuis, Ghent

Universitair Ziekenhuis Leuven, Leuven

Hospital das Clinicas da Faculdade de Medicina da USP, São Paulo

CHU Hopital des enfants, Toulouse

Universitaetsklinikum Essen, Essen

Universitaetsklinikum Freiburg, Freiburg im Breisgau

Azienda Ospedaliera Universitaria Policlinico G. Martino, Messina

Policlinico Univsersitario Agostino Gemelli, Rome

Leids Universitair Medisch Centrum, Leiden

UMC St. Radboud, Nijmegen

Drottning Silvias Barn- ochungdomssjukhus, Gothenburg

Hacettepe University Medical Faculty, Ankara

Sponsors
All Listed Sponsors
lead

BioMarin Pharmaceutical

INDUSTRY