41
Participants
Start Date
January 31, 2013
Primary Completion Date
February 28, 2015
Study Completion Date
July 10, 2017
RP103
Cystagon®
Emory Children's Center, Atlanta
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Baylor College of Medicine / Texas Childrens Hospital, Houston
California Pacific Medical Center (CPMC) Research Institute, San Francisco
Stanford University Medical School, Stanford
University Hospital of Leuven, Leuven
Hospices Civils de Lyon, Lyon
Hôpital Necker-Enfants Malades, Paris
Hôpital Robert Debré, Paris
Ospedale Pediatrico Bambino Gesù, Rome
Radboud University Nijmegen Medical Center, Nijmegen
Queen Elizabeth Hospital Birmingham, Birmingham
Great Ormond Street, London
Guy's Hospital, London
Lead Sponsor
Amgen
INDUSTRY