Safety and Efficacy of EPI-743 in Patients With Friedreich's Ataxia

PHASE2CompletedINTERVENTIONAL
Enrollment

60

Participants

Timeline

Start Date

December 31, 2012

Primary Completion Date

October 31, 2015

Study Completion Date

February 29, 2016

Conditions
Friedreich's Ataxia
Interventions
DRUG

Placebo

Placebo capsules

DRUG

EPI-743 400 mg

DRUG

EPI-743 200 mg

Trial Locations (3)

19104

Childrens Hospital of Philadelphia, Philadelphia

33612

University of South Florida, Tampa

90095

University of California Los Angeles, Los Angeles

Sponsors

Lead Sponsor

All Listed Sponsors
lead

PTC Therapeutics

INDUSTRY

NCT01728064 - Safety and Efficacy of EPI-743 in Patients With Friedreich's Ataxia | Biotech Hunter | Biotech Hunter