60
Participants
Start Date
December 31, 2012
Primary Completion Date
October 31, 2015
Study Completion Date
February 29, 2016
Placebo
Placebo capsules
EPI-743 400 mg
EPI-743 200 mg
Childrens Hospital of Philadelphia, Philadelphia
University of South Florida, Tampa
University of California Los Angeles, Los Angeles
Lead Sponsor
PTC Therapeutics
INDUSTRY