A Placebo-controlled Study of Efficacy & Safety of 2 Trough-ranges of Everolimus as Adjunctive Therapy in Patients With Tuberous Sclerosis Complex (TSC) & Refractory Partial-onset Seizures

PHASE3CompletedINTERVENTIONAL
Enrollment

366

Participants

Timeline

Start Date

April 29, 2013

Primary Completion Date

October 25, 2017

Study Completion Date

October 25, 2017

Conditions
Tuberous Sclerosis Complex-associated Refractory Seizures
Interventions
DRUG

RAD001

Everolimus tablets for oral suspension (dispersible tablets) were packaged as 2 mg tablets in blister packs and placed in boxes with color-coded labels, color 1 or color 2.

DRUG

Placebo

Placebo tablets for oral suspension (dispersible tablets) were packaged as 2 mg tablets in blister packs and placed in boxes with color-coded labels, color 1 or color 2.

DRUG

Antiepileptic drug (1 to 3 only)

no more than any 3 of the listed antiepileptic drugs could be taken with the study drug or placebo. List of allowed antiepileptic drugs were: valporic acid, carbamazepine, clobazam, N-desmethylclobazam, topiramate,TRI477, TRI476, clonazepam, zonisamide, phenobarbital, phenytoin

DRUG

open label RAD001 (only used for post-extension phase)

everolimus tablets for oral suspension (dispersible tablets) were packaged as 2 mg tablets in blister backs in boxes with open label design and were taken during the Post-Extension phase, where all the participants, including those who were previously on placebo, took the 2mg tablets.

Trial Locations (104)

12

Novartis Investigative Site, Dublin

1070

Novartis Investigative Site, Brussels

1090

Novartis Investigative Site, Jette

1145

Novartis Investigative Site, Budapest

1200

Novartis Investigative Site, Brussels

2031

Novartis Investigative Site, Randwick

3000

Novartis Investigative Site, Leuven

3052

Novartis Investigative Site, Parkville

4400

Novartis Investigative Site, Nyíregyháza

6840

Novartis Investigative Site, Perth

7400

Novartis Investigative Site, Kaposvár

9000

Novartis Investigative Site, Ghent

10002

Novartis Investigative Site, Taipei

10016

New York University Medical Center SC-3, New York

10330

Novartis Investigative Site, Bangkok

10400

Novartis Investigative Site, Bangkok

10700

Novartis Investigative Site, Bangkok

12351

Novartis Investigative Site, Berlin

13385

Novartis Investigative Site, Marseille

15236

Novartis Investigative Site, Athens

16147

Novartis Investigative Site, Genova

20080

Novartis Investigative Site, Donostia / San Sebastian

20142

Novartis Investigative Site, Milan

21205

Kennedy Krieger Institute SC, Baltimore

24105

Novartis Investigative Site, Kiel

27100

Novartis Investigative Site, Pavia

28009

Novartis Investigative Site, Madrid

33617

Novartis Investigative Site, Bielefeld

34093

Novartis Investigative Site, Istanbul

35294

University of Alabama at Birmingham SC, Birmingham

38103

LeBonheur Childrens Medical Group SC, Memphis

40133

Novartis Investigative Site, Bologna

41013

Novartis Investigative Site, Seville

44280

Novartis Investigative Site, Guadalajara

46026

Novartis Investigative Site, Valencia

49933

Novartis Investigative Site, Angers

53100

Novartis Investigative Site, Siena

59037

Novartis Investigative Site, Lille

60637

University of Chicago SC - 2, Chicago

63110

Washington University School of Medicine SC-2, St Louis

69677

Novartis Investigative Site, Bron

70124

Novartis Investigative Site, Bari

70421

Novartis Investigative Site, Tainan City

75219

Texas Scottish Rite Hospital for Children Texas Scottish, Dallas

77030

Texas Children s Hospital SC, Houston

The University of Texas Medical School-Houston SC, Houston

77694

Novartis Investigative Site, Kehl-Kork

80045

Children's Hospital Colorado, Aurora

80054

Novartis Investigative Site, Amiens

83301

Novartis Investigative Site, Kaohsiung City

85012

TGen/APNNA, Phoenix

90095

University of California at Los Angeles SC, Los Angeles

92123

Rady Children's Hospital SC, San Diego

94609

Children's Hospital Oakland SC, Oakland

95100

Novartis Investigative Site, Catania

97239

Oregon Health and Science University SC - 3, Portland

119991

Novartis Investigative Site, Moscow

127412

Novartis Investigative Site, Moscow

394024

Novartis Investigative Site, Voronezh

443095

Novartis Investigative Site, Samara

92868-3874

Children's Hospital of Orange County SC, Orange

06106

Connecticut Childrens Medical Center SC, Hartford

02115

Children's Hospital Boston SC, Boston

55102-2383

Minnesota Epilepsy Group - PA SC, Saint Paul

07962

Morristown Memorial Hospital SC-2, Morristown

45229-3039

Cincinnati Children's Hospital Medical Center SC, Cincinnati

19104-4399

Children's Hospital of Philadelphia SC, Philadelphia

C1428AQK

Novartis Investigative Site, CABA

X5000JJS

Novartis Investigative Site, Córdoba

V6H 3V4

Novartis Investigative Site, Vancouver

H3T 1C5

Novartis Investigative Site, Montreal

Unknown

Novartis Investigative Site, Santiago de Cali

Novartis Investigative Site, Bogotá

Novartis Investigative Site, Medellín

8000 C

Novartis Investigative Site, Aarhus

F-67098

Novartis Investigative Site, Strasbourg

455 00

Novartis Investigative Site, Ioannina

00161

Novartis Investigative Site, Roma

700-8558

Novartis Investigative Site, Okayama

594-1101

Novartis Investigative Site, Izumi

565 0871

Novartis Investigative Site, Suita

420-8688

Novartis Investigative Site, Shizuoka

157-8535

Novartis Investigative Site, Setagaya-ku

534-0021

Novartis Investigative Site, Osaka

5591 VE

Novartis Investigative Site, Heeze

3015 CN

Novartis Investigative Site, Rotterdam

3584CX

Novartis Investigative Site, Utrecht

0424

Novartis Investigative Site, Oslo

04 730

Novartis Investigative Site, Warsaw

03080

Novartis Investigative Site, Seoul

05505

Novartis Investigative Site, Seoul

06351

Novartis Investigative Site, Seoul

03722

Novartis Investigative Site, Seoul

08035

Novartis Investigative Site, Barcelona

06100

Novartis Investigative Site, Ankara

06500

Novartis Investigative Site, Ankara

B15 2WB

Novartis Investigative Site, Birmingham

SL9 0RJ

Novartis Investigative Site, Buckinghamshire

CB2 2QQ

Novartis Investigative Site, Cambridge

L12 2AP

Novartis Investigative Site, Liverpool

SW17 0QT

Novartis Investigative Site, London

WC1N 3JH

Novartis Investigative Site, London

S10 2TH

Novartis Investigative Site, Sheffield

YO31 7EX

Novartis Investigative Site, York

Sponsors
All Listed Sponsors
lead

Novartis Pharmaceuticals

INDUSTRY