150
Participants
Start Date
July 31, 2012
Primary Completion Date
July 1, 2019
Study Completion Date
July 1, 2019
Icahn School of Medicine at Mount Sinai, New York
Wake Forest University Health Sciences, Winston-Salem
University of Texas Medical Branch, Galveston
University of Utah, Salt Lake City
University of California, San Francisco, San Francisco
University of Alabama, Birmingham, Birmingham
Rare Diseases Clinical Research Network
NETWORK
Office of Rare Diseases (ORD)
NIH
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
NIH
Icahn School of Medicine at Mount Sinai
OTHER