Efficacy and Safety Study of Velaglucerase Alfa in Children and Adolescents With Type 3 Gaucher Disease

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

7

Participants

Timeline

Start Date

September 14, 2012

Primary Completion Date

March 15, 2015

Study Completion Date

March 15, 2015

Conditions
Gaucher Disease, Type 3
Interventions
BIOLOGICAL

velaglucerase alfa

lyophilized powder, intravenous infusion, units, Every other week (EOW)

Trial Locations (5)

1007

Hospital La Rabta, Tunis

21131

Alexandria University Hospital, Alexandria

Unknown

Abu El Rich Hospital, Cairo University Hospital, Cairo

Children's Hospital, Ain Shams University Hospital, Cairo

KEM Hospital Research Centre, Pune

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Shire

INDUSTRY