NCT01645787View on ClinicalTrials.gov

Short and Long Term Treatment With 4-AP in Ambulatory SMA Patients

PHASE2/PHASE3CompletedINTERVENTIONAL
Enrollment

11

Participants

Timeline

Start Date

June 1, 2012

Primary Completion Date

September 30, 2015

Study Completion Date

September 30, 2015

Conditions
Spinal Muscular Atrophy
Interventions
DRUG

4-aminopyridine

10 mg/twice daily

DRUG

Placebo

Crossover study involving one trial with sugar pill (placebo)

Trial Locations (1)

10032

Columbia University Medical Center, New York

All Listed Sponsors
collaborator

United States Department of Defense

FED

lead

Columbia University

OTHER

NCT01645787 - Short and Long Term Treatment With 4-AP in Ambulatory SMA Patients | Biotech Hunter | Biotech Hunter