A Retrospective, Observational, Noninterventional Data Collection Study for Patients With Molybdenum Cofactor Deficiency Who Have Been Previously Treated With Cyclic Pyranopterin Monophosphate (cPMP)

CompletedOBSERVATIONAL
Enrollment

15

Participants

Timeline

Start Date

November 30, 2012

Primary Completion Date

October 31, 2014

Study Completion Date

October 31, 2014

Conditions
Molybdenum Cofactor Deficiency
Trial Locations (13)

37232

Vanderbilt Children's Hospital, Nashville

53226

Children's Hospital of Wisconsin, Milwaukee

Unknown

Neonatologist, Department of Paediatrics, Mercy Hospital for Women, Heidelberg

Monash Medical Centre, Melbourne

Western Sydney Genetics Program & Sydney Medical School, Westmead

University Hospital of Cologne, Cologne

Frankfurt Children's Hospital, Frankfurt

Akademisches Lehrkrankenhaus der Johannes Gutenberg, Koblenz

Beatrix Children's Hospital, Groningen

TC Saglik Bakanligi Gaziantep Cocuk Hastaliklari Hastanesi, Gaziantep

Birmingham Children's Hospital, Birmingham

Royal Hospital for Sick Children, Glasgow

Manchester Academic Health Science Centre, Manchester

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Origin Biosciences

INDUSTRY