Phase I Clinical Trial of ManNAc in Patients With GNE Myopathy or Hereditary Inclusion Body Myopathy (HIBM)

PHASE1CompletedINTERVENTIONAL
Enrollment

26

Participants

Timeline

Start Date

September 11, 2012

Study Completion Date

May 29, 2013

Conditions
Hereditary Inclusion Body Myopathy (HIBM)GNE Myopathy
Interventions
DRUG

ManNAc

Single dose

Trial Locations (1)

20892

National Institutes of Health Clinical Center, 9000 Rockville Pike, Bethesda

All Listed Sponsors
collaborator

National Center for Advancing Translational Sciences (NCATS)

NIH

collaborator

Therapeutics for Rare and Neglected Diseases (TRND)

NIH

lead

National Human Genome Research Institute (NHGRI)

NIH

NCT01634750 - Phase I Clinical Trial of ManNAc in Patients With GNE Myopathy or Hereditary Inclusion Body Myopathy (HIBM) | Biotech Hunter | Biotech Hunter