Study of SDMB (2,2 Dimethylbutyrate, Sodium Salt) in Beta Thalassemia Intermedia in Thailand

PHASE2CompletedINTERVENTIONAL
Enrollment

10

Participants

Timeline

Start Date

March 31, 2012

Primary Completion Date

November 30, 2012

Study Completion Date

December 31, 2012

Conditions
Beta Thalassemia Intermedia
Interventions
DRUG

sodium 2,2 dimethylbutyrate

Oral capsule, dose 20 mg/kg/day, daily, for 26 weeks

Trial Locations (1)

Unknown

Mahidol University Thalassemia Research Centre, Nakhonpathom

All Listed Sponsors
collaborator

Mahidol University

OTHER

lead

Boston University

OTHER

NCT01609595 - Study of SDMB (2,2 Dimethylbutyrate, Sodium Salt) in Beta Thalassemia Intermedia in Thailand | Biotech Hunter | Biotech Hunter