A Multicenter, Multinational Clinical Assessment Study for Pediatric Patients With Achondroplasia

CompletedOBSERVATIONAL
Enrollment

363

Participants

Timeline

Start Date

April 30, 2012

Primary Completion Date

February 28, 2021

Study Completion Date

February 28, 2021

Conditions
Achondroplasia
Trial Locations (20)

2145

The Children's Hospital at Westmead, Westmead

3052

Murdoch Children's Research Institute, Parkville

19803

Nemours/Alfred I. duPont Hospital for Children, Wilmington

29010

Hospital Universitario Virgen de la Victoria, Málaga

30033

Emory University, Decatur

34752

Acibadem University School of Medicine, Istanbul

37232

Vanderbilt University, Nashville

45229

Cincinnati Children's Hospital Medical Center, Cincinnati

53226

Medical College of Wisconsin, Children's Hospital, Milwaukee

60614

Ann and Robert H Lurie Children's Hospital of Chicago, Chicago

77030

Baylor College of Medicine, Houston

90048

Harbor-UCLA Medical Center, Los Angeles

94609

Children's Hospital and Research Center Oakland, Oakland

Unknown

Osaka University Hospital, Osaka

Saitama Children's Medical Center, Saitama

Tokushima University Hospital, Tokushima

08028

Institut Catala de Traumatologica I Medicina de l'Esport, Barcelona

08950

Hospital Sant Joan de Deu Barcelona, Barcelona

SE1 9RT

Guy's and St. Thomas NHS Foundation Trust Evelina Children's Hospital, London

S10 2TH

Sheffield Children's NHS Foundation Trust, Sheffield

Sponsors
All Listed Sponsors
lead

BioMarin Pharmaceutical

INDUSTRY