363
Participants
Start Date
April 30, 2012
Primary Completion Date
February 28, 2021
Study Completion Date
February 28, 2021
The Children's Hospital at Westmead, Westmead
Murdoch Children's Research Institute, Parkville
Nemours/Alfred I. duPont Hospital for Children, Wilmington
Hospital Universitario Virgen de la Victoria, Málaga
Emory University, Decatur
Acibadem University School of Medicine, Istanbul
Vanderbilt University, Nashville
Cincinnati Children's Hospital Medical Center, Cincinnati
Medical College of Wisconsin, Children's Hospital, Milwaukee
Ann and Robert H Lurie Children's Hospital of Chicago, Chicago
Baylor College of Medicine, Houston
Harbor-UCLA Medical Center, Los Angeles
Children's Hospital and Research Center Oakland, Oakland
Osaka University Hospital, Osaka
Saitama Children's Medical Center, Saitama
Tokushima University Hospital, Tokushima
Institut Catala de Traumatologica I Medicina de l'Esport, Barcelona
Hospital Sant Joan de Deu Barcelona, Barcelona
Guy's and St. Thomas NHS Foundation Trust Evelina Children's Hospital, London
Sheffield Children's NHS Foundation Trust, Sheffield
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY