1,147
Participants
Start Date
March 31, 2012
Primary Completion Date
August 31, 2016
Study Completion Date
June 30, 2017
University of Minnesota, Minneapolis
Children's Hospital of Orange County, Orange
Rare Diseases Clinical Research Network
NETWORK
National Center for Advancing Translational Sciences (NCATS)
NIH
National Institute of Neurological Disorders and Stroke (NINDS)
NIH
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
NIH
University of Minnesota
OTHER