G551D Observational Study- Expanded to Additional Genotypes and Extended for Long Therm Follow up (GOAL-e2)

CompletedOBSERVATIONAL
Enrollment

120

Participants

Timeline

Start Date

January 31, 2014

Primary Completion Date

June 30, 2021

Study Completion Date

June 30, 2021

Conditions
Cystic Fibrosis
Trial Locations (36)

14222

Women and Children's Hospital of Buffalo, Buffalo

15213

Children's Hospital of Pittsburgh of UPMC- University of Pittsburgh, Pittsburgh

21287

The Johns Hopkins University, Baltimore

26506

West Virginia University CF Medical Center, Morgantown

27599

University of North Carolina at Chapel Hill, Chapel Hill

29403

Medical University of South Carolina, Charleston

35233

University of Alabama at Birmingham, Birmingham

44106

University Hospitals Case Medical Center/Rainbow Babies and Children's Hospital, Cleveland

45229

Cincinnati Children's Hospital Medical Center, Cincinnati

46202

Riley Hospital for Children Indiana University Medical Center, Indianapolis

48201

Children's Hospital of Michigan, Detroit

49503

Grand Rapids CF Center, Grand Rapids

55455

University of Minnesota, Minneapolis

60637

University of Chicago, Chicago

64108

The Children's Mercy Hospital--University of Missouri at Kansas City, Kansas City

77030

Baylor College of Medicine/Texas Children's Hospital, Houston

80045

The Children's Hospital Colarado, Aurora

80206

National Jewish Health, Denver

84132

Intermountain Cystic Fibrosis Center University of Utah Health Sciences Center, Salt Lake City

94394

Stanford University Medical Center, Palo Alto

97239

Oregon Health Sciences University, Portland

Unknown

Phoenix Childrens Hospital, Phoenix

University of Arkansas for Medical Sciences, Little Rock

Yale, New Haven

Indianapolis University, Indianapolis

University of Kentucky, Lexington

University of Michigan, Ann Arbor

Dartmouth Hitchcock Clinic-Lebanon, Lebanon

Nation Wide Childrens Hospital, Columbus

Toledo Children's Hospital, Toledo

Children's Hospital of Philadelphia, Philadelphia

Froedtert & Medical College of Wisconsin, Milwaukee

02114

Massachusetts General Hospital, Boston

02115

Children's Hospital Boston, Boston

37232-9500

Vanderbilt Children's Hospital Vanderbilt University Medical Center, Nashville

75390-8558

University of Texas Southwestern/Children's Medical Center of Dallas, Dallas

All Listed Sponsors
lead

Steven M Rowe

OTHER

NCT01521338 - G551D Observational Study- Expanded to Additional Genotypes and Extended for Long Therm Follow up (GOAL-e2) | Biotech Hunter | Biotech Hunter