Study of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome)

PHASE2CompletedINTERVENTIONAL
Enrollment

15

Participants

Timeline

Start Date

October 31, 2011

Primary Completion Date

February 29, 2016

Study Completion Date

February 29, 2016

Conditions
Mucopolysaccharidosis IVAMorquio A SyndromeMPS IVA
Interventions
DRUG

BMN 110

Patients will receive intravenous (IV) infusions of study drug at a dose of 2.0 mg/kg/wk over a period of approximately 4 hours every week for up to 208 weeks.

Trial Locations (5)

Unknown

Oakland

Manhasset

Monza

Taipei

Central Manchester

Sponsors
All Listed Sponsors
lead

BioMarin Pharmaceutical

INDUSTRY