NCT01510028View on ClinicalTrials.gov

Multicenter Study of HGT-1110 Administered Intrathecally in Children With Metachromatic Leukodystrophy (MLD)

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

24

Participants

Timeline

Start Date

February 2, 2012

Primary Completion Date

January 20, 2017

Study Completion Date

January 20, 2017

Conditions
Metachromatic Leukodystrophy (MLD)
Interventions
BIOLOGICAL

Recombinant human arylsulfatase A

6 patients treated with HGT-1110 EOW by IT injection

Trial Locations (5)

2100

Rigshospitalet, Copenhagen

2145

The Children's Hospital at Westmead, Westmead

72076

Center for Pediatric Clinical Studies, Tübingen

94275

Hopital de Bicetre, Le Kremlin-Bicêtre

565-0871

Osaka University Hospital, Suita

Sponsors

Lead Sponsor

Shire
All Listed Sponsors
lead

Shire

INDUSTRY