6
Participants
Start Date
August 31, 2011
Primary Completion Date
August 31, 2013
Study Completion Date
August 31, 2019
Subretinal administration of rAAV2-VMD2-hMERTKRecombinant Adeno-Associated Virus
The study is an open-label, dose-escalation, phase I clinical trial of subretinal administration of rAAV2-VMD2-hMERTK in patients with retinitis pigmentosa due to MERTK mutation.
King Khaled Eye Specialist Hospital, Riyadh
King Faisal Specialist Hospital & Research Center
OTHER
King Khaled Eye Specialist Hospital
OTHER_GOV