53
Participants
Start Date
July 31, 2012
Primary Completion Date
August 31, 2017
Study Completion Date
August 31, 2017
Royal Children's Hospital, Melborne
Children's Hospital of Pittsburgh of UPMC, Pittsburgh
Children's National Medical Center, Washington D.C.
Duke Children's Hospital, Durham
Carolinas Medical Center, Charlotte
University of Minnesota, Minneapolis
Washington University, St Louis
University of California - Davis, Sacramento
The Children's Hospital at Westmead, Sydney
Alberta Children's Hospital, Calgary
Queen Silvia Children's Hospital, Gothenburg
Newcastle University, Newcastle upon Tyne
Collaborators (1)
FSH Society, Inc.
INDUSTRY
FSHD Global Research Foundation
OTHER
Muscular Dystrophy Canada
OTHER
aTyr Pharma, Inc.
INDUSTRY
Cooperative International Neuromuscular Research Group
NETWORK