21
Participants
Start Date
August 15, 2011
Primary Completion Date
September 9, 2016
Study Completion Date
September 9, 2016
BMN 701
GILT-tagged recombinant human GAA
Auckland City and Starship Children's Hospital, Auckland
Royal Brisbane and Women's Hospital, Herston
Royal Adelaide Hospital, North Adelaide
University of Florida College of Medicine, Gainesville
Tampa General Hospital, Tampa
Villa Metabolica, ZKJM MC University Mainz, Mainz
University of Kansas Medical Center, Kansas City
Hôpital Pitié-Salpêtrière, Paris
Univ of California San Diego School of Medicine, San Diego
University Hospitals Birmingham NHS Foundation Trust, Birmingham
Royal Free Hospital, London
Salford Royal NHS Foundation Trust, Salford
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY