Neuroimaging and Neurocognitive Assessment and Response to Sapropterin Dihydrochloride Treatment in Phenylketonuria

NAWithdrawnINTERVENTIONAL
0
Timeline

Start Date

April 30, 2011

Primary Completion Date

March 31, 2012

Study Completion Date

December 31, 2012

Conditions
PKU
Interventions
DIETARY_SUPPLEMENT

diet

12 participants will be randomized to diet. Phe levels will be followed by blood levels. A dietician will analyze diet for phe content and advise

DRUG

sapropterin dihydrochloride

20 mg/kg for 4 months

DRUG

sapropterin dihydrochloride

Trial Locations (1)

20010

Children's Research Institute, Washington D.C.

All Listed Sponsors
collaborator

Georgetown University

OTHER

lead

Children's National Research Institute

OTHER