NCT01379625View on ClinicalTrials.gov

Study of Triheptanoin for Treatment of Long-Chain Fatty Acid Oxidation Disorder

PHASE2CompletedINTERVENTIONAL
Enrollment

32

Participants

Timeline

Start Date

September 30, 2011

Primary Completion Date

April 30, 2015

Study Completion Date

April 30, 2015

Conditions
Very Long-chain acylCoA Dehydrogenase (VLCAD) DeficiencyCarnitine Palmitoyltransferase 2 (CPT2) DeficiencyMitochondrial Trifunctional Protein (TFP) DeficiencyLong-chain 3 hydroxyacylCoA Dehydrogenase (LCHAD) Deficiency
Interventions
DRUG

Triheptanoin

Triglyceride with three heptanoin or 7 carbon fatty acids esterified to a glycerol backbone

Trial Locations (2)

15224

University of Pittsburgh, Pittsburgh

97239

Oregon Health & Science University, Portland

All Listed Sponsors
collaborator

University of Pittsburgh

OTHER

lead

Oregon Health and Science University

OTHER

NCT01379625 - Study of Triheptanoin for Treatment of Long-Chain Fatty Acid Oxidation Disorder | Biotech Hunter | Biotech Hunter