6
Participants
Start Date
March 31, 2011
Primary Completion Date
November 13, 2019
Study Completion Date
November 13, 2019
Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene
transplantation of patient's autologous CD34+ cells transduced with lentiviral vector containing human WAS gene
Great Ormond Street Hospital, London
Royal Free Hospital, London
Lead Sponsor
Great Ormond Street Hospital for Children NHS Foundation Trust
OTHER
Institute of Child Health
OTHER
Genethon
OTHER