1
Participants
Start Date
October 31, 2008
Primary Completion Date
March 31, 2010
Study Completion Date
April 30, 2010
rhARSA
intravenous infusion 100U/kg every other week for 18 months
Department of Pediatric Endocrinology and Neurology, Saint Vincent de Paul Hospital, Paris
Collaborators (1)
European Leukodystrophy Association
OTHER
Zymenex A/S
INDUSTRY
Shire
INDUSTRY
Assistance Publique - Hôpitaux de Paris
OTHER