Efficacy METAZYM for the Treatment Metachromatic Leukodystrophy Treated With Hematopoietic Stem Cell Transplantation

PHASE2CompletedINTERVENTIONAL
Enrollment

1

Participants

Timeline

Start Date

October 31, 2008

Primary Completion Date

March 31, 2010

Study Completion Date

April 30, 2010

Conditions
Metachromatic Leukodystrophy
Interventions
DRUG

rhARSA

intravenous infusion 100U/kg every other week for 18 months

Trial Locations (1)

75014

Department of Pediatric Endocrinology and Neurology, Saint Vincent de Paul Hospital, Paris

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

European Leukodystrophy Association

OTHER

collaborator

Zymenex A/S

INDUSTRY

collaborator

Shire

INDUSTRY

lead

Assistance Publique - Hôpitaux de Paris

OTHER

NCT01303146 - Efficacy METAZYM for the Treatment Metachromatic Leukodystrophy Treated With Hematopoietic Stem Cell Transplantation | Biotech Hunter | Biotech Hunter