Safety/Tolerability/Pharmacokinetic (PK)/Pharmacodynamics (PD) Study of BMN701 in Patients With Late-Onset Pompe Disease

Royal Adelaide Hospital, SA Pathology, Adelaide

University of Florida College of Medicine, Gainesville

Zentrum für Kinder- und Jugenmedizin, Mainz

University of Kansas Medical Center, Kansas City

Hôpital Pitié-Salpêtrière, Paris

Univ of California San Diego School of Medicine, La Jolla

Hôpital de I´Archet- Centre Hospitalier Universitaire Nice, Nice

Old Queen Elizabeth Hospital, Department of Medicine, Birmingham

Royal Free Hospital, London

Salford Royal Hospital NHS Trust, Salford