Natural History Study of SCID Disorders

Enrolling by invitationOBSERVATIONAL
Enrollment

690

Participants

Timeline

Start Date

September 2, 2010

Primary Completion Date

September 30, 2028

Study Completion Date

September 30, 2028

Conditions
Severe Combined Immunodeficiency (SCID)Leaky SCIDOmenn SyndromeReticular DysgenesisADA SCIDXSCID
Trial Locations (44)

10065

Memorial Sloan-Kettering Cancer Center, New York

10595

New York Medical College, Maria Fareri Children's Hospital, Valhalla

14642

University of Rochester Medical Center/ Golisano Children's Hospital, Rochester

15224

Children's Hospital of Pittsburgh of UPMC, Pittsburgh

19104

The Children's Hospital of Philadelphia, Philadelphia

19803

Alfred I. duPont Hospital for Children/Nemours, Wilmington

20892

NIH Clinical Center Genetic Immunotherapy Section, Bethesda

27710

Duke University, Durham

30322

Children's Healthcare of Atlanta/Emory University School of Medicine, Atlanta

33701

Johns Hopkins All Children's Hospital, St. Petersburg

35233

University of Alabama at Birmingham, Birmingham

38105

St. Jude Children's Research Hospital, Memphis

43205

Nationwide Children's Hospital, Columbus

44106

University Hospitals-Rainbow Babies and Children's Hospital, Cleveland

45229

Cincinnati Children's Hospital Medical Center, Cincinnati

48109

University of Michigan Health System, Ann Arbor

55455

University of Minnesota Medical Center, Minneapolis

55905

Mayo Clinic Hospital, Rochester

60614

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago

63104

Cardinal Glennon Children's Medical Center, St Louis

63110

Washington University St Louis Children's Hospital, St Louis

70118

Children's Hospital/Louisiana State University Health Sciences Center, New Orleans

78229

Methodist Children's Hospital of South Texas/Texas Transplant Institute, San Antonio

80220

Children's Hospital Denver, Denver

84113

Primary Children's Medical Center/University of Utah, Salt Lake City

85016

Phoenix Children's Hospital, Phoenix

90027

Children's Hospital Los Angeles, Los Angeles

94304

Lucile Salter Packard Children's Hospital at Stanford, Palo Alto

98101

Seattle Children's Research Institute, Seattle

90095-1752

University of California, Los Angeles, Los Angeles

94143-1278

University of California San Francisco Children's Hospital, San Francisco

20010-2970

Children's National Medical Center, Washington D.C.

02115

Children's Hospital Boston, Boston

07601

Hackensack University Medical Center, Hackensack

97239-3098

Oregon Health and Science University, Portland

75390-9263

University of Texas Southwestern Medical Center/Children's of Dallas, Dallas

77030-2399

Texas Children's Hospital, Houston

53705-2275

University of Wisconsin/ American Family Children's Hospital, Madison

53226-4874

Medical College of Wisconsin, Milwaukee

T3B 6A8

Alberta Children's Hospital, Calgary

V6H 3V4

British Columbia Children's Hospital, Vancouver

R3E 0V9

Cancer Care Manitoba, Winnipeg

M5G 1XB

The Hospital for Sick Children, Toronto

H3T 1C5

CHU Sainte-Justine, Montreal

All Listed Sponsors
collaborator

Primary Immune Deficiency Treatment Consortium (PIDTC)

OTHER

collaborator

Office of Rare Diseases (ORD)

NIH

collaborator

National Center for Advancing Translational Sciences (NCATS)

NIH

lead

National Institute of Allergy and Infectious Diseases (NIAID)

NIH

NCT01186913 - Natural History Study of SCID Disorders | Biotech Hunter | Biotech Hunter