690
Participants
Start Date
September 2, 2010
Primary Completion Date
September 30, 2028
Study Completion Date
September 30, 2028
Memorial Sloan-Kettering Cancer Center, New York
New York Medical College, Maria Fareri Children's Hospital, Valhalla
University of Rochester Medical Center/ Golisano Children's Hospital, Rochester
Children's Hospital of Pittsburgh of UPMC, Pittsburgh
The Children's Hospital of Philadelphia, Philadelphia
Alfred I. duPont Hospital for Children/Nemours, Wilmington
NIH Clinical Center Genetic Immunotherapy Section, Bethesda
Duke University, Durham
Children's Healthcare of Atlanta/Emory University School of Medicine, Atlanta
Johns Hopkins All Children's Hospital, St. Petersburg
University of Alabama at Birmingham, Birmingham
St. Jude Children's Research Hospital, Memphis
Nationwide Children's Hospital, Columbus
University Hospitals-Rainbow Babies and Children's Hospital, Cleveland
Cincinnati Children's Hospital Medical Center, Cincinnati
University of Michigan Health System, Ann Arbor
University of Minnesota Medical Center, Minneapolis
Mayo Clinic Hospital, Rochester
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Cardinal Glennon Children's Medical Center, St Louis
Washington University St Louis Children's Hospital, St Louis
Children's Hospital/Louisiana State University Health Sciences Center, New Orleans
Methodist Children's Hospital of South Texas/Texas Transplant Institute, San Antonio
Children's Hospital Denver, Denver
Primary Children's Medical Center/University of Utah, Salt Lake City
Phoenix Children's Hospital, Phoenix
Children's Hospital Los Angeles, Los Angeles
Lucile Salter Packard Children's Hospital at Stanford, Palo Alto
Seattle Children's Research Institute, Seattle
University of California, Los Angeles, Los Angeles
University of California San Francisco Children's Hospital, San Francisco
Children's National Medical Center, Washington D.C.
Children's Hospital Boston, Boston
Hackensack University Medical Center, Hackensack
Oregon Health and Science University, Portland
University of Texas Southwestern Medical Center/Children's of Dallas, Dallas
Texas Children's Hospital, Houston
University of Wisconsin/ American Family Children's Hospital, Madison
Medical College of Wisconsin, Milwaukee
Alberta Children's Hospital, Calgary
British Columbia Children's Hospital, Vancouver
Cancer Care Manitoba, Winnipeg
The Hospital for Sick Children, Toronto
CHU Sainte-Justine, Montreal
Primary Immune Deficiency Treatment Consortium (PIDTC)
OTHER
Office of Rare Diseases (ORD)
NIH
National Center for Advancing Translational Sciences (NCATS)
NIH
National Institute of Allergy and Infectious Diseases (NIAID)
NIH