191
Participants
Start Date
August 12, 2010
Primary Completion Date
December 2, 2013
Study Completion Date
December 2, 2013
Ataluren
Ataluren will be provided as a vanilla-flavored powder to be mixed with water or milk.
St. Vincent's Hospital, New York
New York Medical College, Valhalla
Childrens Hospital of Pittsburgh, Pittsburgh
Johns Hopkins Children's Center, Baltimore
University of North Carolina, Chapel Hill
Emory University Cystic Fibrosis Center, Atlanta
Hôpital des Enfants, Toulouse
University of Miami, Miami
University of Alabama-Birmingham, Birmingham
Rainbow Babies & Children's Hospital, Cleveland
Children's Memorial Hospital, Chicago
Washington University, St Louis
The Children's Hospital, Aurora
Miller Children's Hospital Long Beach, Long Beach
Hadassah University Hospital - Mount Scopus, Jerusalem
Lucile Packard Children's Hospital, Palo Alto
Children's Hospital Boston, Boston
Hôpital Erasme, Brussels
Hôpital Universitaire des Enfants Reine Fabiola, Brussels
University Hospital Brussels, Brussels
University Hospital Leuven, Leuven
University of Toronto, Toronto
Hôpital Cochin, Paris
Hôpital Necker - Enfants Malades, Paris
Klinikum der Universität Köln, Cologne
Università La Sapienza, Roma
Azienda Ospedaliera di Verona, Verona
Universitair Medisch Centrum Utrecht, Utrecht
Hospital Universitario La Paz, Madrid
Karolinska University Hospital, Huddinge, Stockholm
Belfast City Hospital, Belfast
Lead Sponsor
Cystic Fibrosis Foundation
OTHER
PTC Therapeutics
INDUSTRY