Efficacy of Eltrombopag to Improve Thrombocytopenia of MYH9-related Disease

PHASE2CompletedINTERVENTIONAL
Enrollment

12

Participants

Timeline

Start Date

January 31, 2009

Primary Completion Date

June 30, 2010

Study Completion Date

June 30, 2010

Conditions
Blood Platelet Disorders
Interventions
DRUG

eltrombopag

Eltrombopag, administered orally, 50 mg/daily for 21 days. Patients with platelet counts between 100 and 150x10e9/L at day 21 will continue eltrombopag 50 mg/daily for 21 additional days. Patients with platelet count lower than 100x10e9/L at day 21 will receive eltrombopag 75 mg/daily for additional 21 days. Patients with more than 150x10e9 platelets/L at day 21 will stop therapy.

Trial Locations (3)

27100

Fondazione IRCCS Policlinico San Matteo, Unità di Medicina III, Pavia

35128

Azienda Ospedaliero-Universitaria di Padova, Unità di Medicina Generale e Patologia Speciale, Padua

06122

Policlinico Monteluce, Sezione di Medicina Interna e Cardiovascolare, Perugia

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

University of Pavia

OTHER

collaborator

GlaxoSmithKline

INDUSTRY

collaborator

Azienda Ospedaliera di Padova

OTHER

collaborator

Azienda Ospedaliera di Perugia

OTHER

collaborator

Fondazione Telethon

OTHER

lead

Fondazione IRCCS Policlinico San Matteo di Pavia

OTHER