6
Participants
Start Date
January 13, 2010
Primary Completion Date
March 23, 2010
Study Completion Date
March 23, 2010
Ataluren
Oral powder
Chronic Corticosteroid Therapy
Enrollment was stratified to ensure evaluation of approximately half of the participants were receiving chronic corticosteroid therapy and approximately half of participants were not receiving chronic corticosteroid therapy. Therefore, 3 out of 6 participants were receiving chronic corticosteriod therapy. For the participants receiving chronic corticosteriod therapy, a stable corticosteriod regimen was to be maintained during the study.
Nationwide Children's Hospital, Columbus
University of Minnesota, Minneapolis
Washington University Medical School, St Louis
University of California-Davis, Davis
Children's Hospital of Boston, Boston
University of Newcastle, Newcastle upon Tyne
Lead Sponsor
Genzyme, a Sanofi Company
INDUSTRY
PTC Therapeutics
INDUSTRY