Fetal Umbilical Cord Blood (UCB) Transplant for Lysosomal Storage Diseases

PHASE1WithdrawnINTERVENTIONAL
0
Timeline

Start Date

October 31, 2009

Primary Completion Date

March 31, 2017

Study Completion Date

March 31, 2017

Conditions
Lysosomal Storage DiseasesInborn Errors of Metabolism
Interventions
BIOLOGICAL

ALD-601

ALD-601 is manufactured by Aldagen from the 20% compartment of the selected umbilical cord blood unit within 24 hrs of planned injection. A dose of ALD-601 that delivers 1 x 105 - 2 x 106 cells/kg of estimated fetal weight at day - 1 is suspended in 300 microliters of dialysis media.

Trial Locations (2)

27705

Duke University Medical Center Pediatric Blood and Marrow Transplant, Durham

Duke University Medical Center, Durham

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

Aldagen

INDUSTRY

lead

Joanne Kurtzberg, MD

OTHER

NCT01003912 - Fetal Umbilical Cord Blood (UCB) Transplant for Lysosomal Storage Diseases | Biotech Hunter | Biotech Hunter