14
Participants
Start Date
February 22, 2010
Primary Completion Date
December 31, 2025
Study Completion Date
December 31, 2025
Gene Transfer
Peripheral vein infusion of scAAV2/8-LP1-hFIXco vector once per participant
scAAV2/8-LP1-hFIXco
Peripheral vein infusion of scAAV2/8-LP1-hFIXco vector once per participant.
Hemophilia Center of Western Pennsylvania, Pittsburgh
St. Jude Children's Research Hospital, Memphis
University of Kentucky, Lexington
Scott and White Memorial Hospital, Temple
Stanford Medical School, Stanford
Oregon Health and Science University, Portland
University of Texas Southwestern, Dallas
Katharine Dormandy Haemophilia Centre and Haemostasis Unit, University College of London, London
National Heart, Lung, and Blood Institute (NHLBI)
NIH
Hemophilia of Georgia, Inc.
OTHER
Children's Hospital of Philadelphia
OTHER
University College, London
OTHER
St. Jude Children's Research Hospital
OTHER