20
Participants
Start Date
August 31, 2009
Primary Completion Date
August 31, 2010
Study Completion Date
August 31, 2011
Sapropterin
Sapropterin (Kuvan) 20mg/kg/day taken once daily or as otherwise prescribed by physician as standard care.
University of Missouri, Columbia
Collaborators (1)
BioMarin Pharmaceutical
INDUSTRY
University of Missouri-Columbia
OTHER