Study of cPMP (Precusor Z) to Treat Molybdenum Cofactor Deficiency (MoCD) Type A

PHASE1/PHASE2WithdrawnINTERVENTIONAL
Enrollment

10

Participants

Timeline

Start Date

August 31, 2009

Primary Completion Date

April 30, 2010

Conditions
Molybdenum Cofactor Deficiency Type A
Interventions
DRUG

cPMP

Intravenous solution administered daily. Dose titrated from 80 μg/kg on Days 1-12 to 120 μg/kg on Days 13-34 to 160 μg/kg for days 35-90.

Trial Locations (1)

3168

Monash Medical Centre, Melbourne

All Listed Sponsors
lead

Orphatech Pharmaceuticals, GmbH

INDUSTRY

NCT00957749 - Study of cPMP (Precusor Z) to Treat Molybdenum Cofactor Deficiency (MoCD) Type A | Biotech Hunter | Biotech Hunter