13
Participants
Start Date
October 14, 2009
Primary Completion Date
August 30, 2011
Study Completion Date
August 30, 2011
Ataluren
Oral powder
Children's Hospital of Philadelphia, Philadelphia
Vanderbilt Hemostatis and Thrombosis Clinic, Nashville
Cincinnati Children's Hospital Medical Center, Cincinnati
St. Vincent Indianapolis Hospital, Indianapolis
The Bleeding and Clotting Disorders Institute, Peoria
Puget Sound Blood Center, Seattle
New England Hemophilia Center, Worcester
St. Paul's Hospital, Vancouver
Hôpital Cardiologique, Lille
Hôpital Edouard Herriot, Lyon
Hôpital Necker Enfants Malades, Paris
Azienda Ospedaliero-Universitaria Careggi Viale G.B. Morgagni, Florence
A.Bianchi Bonomi Hemophilia and Thrombosis Center, Milan
Lead Sponsor
Genzyme, a Sanofi Company
INDUSTRY
PTC Therapeutics
INDUSTRY