173
Participants
Start Date
January 31, 2009
Primary Completion Date
May 24, 2010
Study Completion Date
May 24, 2010
Ataluren
Ataluren oral powder for suspension will be administered as per dose and schedule specified in the arm.
The Children's Hospital at Westmead, Westmead
The Royal Children's Hospital, Parkville
Columbia University, New York
Hopital d'Enfants CHU Timone, Marseille
Children's Hospital of Philadelphia, Philadelphia
Ospedale Maggiore Policlinico, Mangiagalli e Regina Elena, Milan
Duke University Medical Center, Durham
Child Neurology Center of NW Florida, Gulf Breeze
Cincinnati Children's Hospital Medical Center, Cincinnati
University of Iowa Children's Hospital, Division of Child Neurology, Iowa City
University of Minnesota, Minneapolis
Washington University Medical School, St Louis
University of Kansas Medical Center, Kansas City
Southwestern University, Dallas
Department of Rehabilitation, The Children's Hospital, Aurora
University of Utah, Salt Lake City
University of California - Davis, Sacramento
Shriners Hospital for Children-Portland, Portland
Children's Hospital of Boston, Boston
UZ Leuven, Leuven
Alberta Children's Hospital, London
Children's Hospital of Western Ontario, London
British Colombia Children's Hopsital, Vancouver
Laboratoire d'Exploration Fonctionnelles, Nantes
Groupe Hospitalier Pitie-Salpetriere, Institut de Myologie, Paris
University of Essen - Clinic for Children, Essen
University Hospital, Freiburg im Breisgau
Hadassah University Hopspital, Jerusalem
Hospital Sant Joan de Deu, Barcelona
Hospital Universitario La Fe, Valencia
Astrid Lindgren Pediatric Hospital, Stockholm
UCL Instititute of Child Health, Dubowitz, London
University of Newcastle, Newcastle upon Tyne
Robert Jones & Agnes Hunt Orthopaedic Hospital, Oswestry
Ospedale Pediatrico Bambino Gesu, Roma
U.O. Complessa di Neuropsichiatria Infantile-Policlinico A. Gemelli-Universita Cattolica, Roma
Queen Silvia Children's Hospital, Gothenburg
Lead Sponsor
Genzyme, a Sanofi Company
INDUSTRY
PTC Therapeutics
INDUSTRY