Phase 2B Extension Study of Ataluren (PTC124) in Duchenne/Becker Muscular Dystrophy (DMD/BMD)

PHASE2TerminatedINTERVENTIONAL
Enrollment

173

Participants

Timeline

Start Date

January 31, 2009

Primary Completion Date

May 24, 2010

Study Completion Date

May 24, 2010

Conditions
Duchenne Muscular DystrophyBecker Muscular Dystrophy
Interventions
DRUG

Ataluren

Ataluren oral powder for suspension will be administered as per dose and schedule specified in the arm.

Trial Locations (37)

2145

The Children's Hospital at Westmead, Westmead

3052

The Royal Children's Hospital, Parkville

10032

Columbia University, New York

13385

Hopital d'Enfants CHU Timone, Marseille

19104

Children's Hospital of Philadelphia, Philadelphia

20122

Ospedale Maggiore Policlinico, Mangiagalli e Regina Elena, Milan

27710

Duke University Medical Center, Durham

32561

Child Neurology Center of NW Florida, Gulf Breeze

45229

Cincinnati Children's Hospital Medical Center, Cincinnati

52242

University of Iowa Children's Hospital, Division of Child Neurology, Iowa City

55414

University of Minnesota, Minneapolis

63110

Washington University Medical School, St Louis

66160

University of Kansas Medical Center, Kansas City

75207

Southwestern University, Dallas

80045

Department of Rehabilitation, The Children's Hospital, Aurora

84112

University of Utah, Salt Lake City

95817

University of California - Davis, Sacramento

97239

Shriners Hospital for Children-Portland, Portland

02115

Children's Hospital of Boston, Boston

Unknown

UZ Leuven, Leuven

Alberta Children's Hospital, London

Children's Hospital of Western Ontario, London

British Colombia Children's Hopsital, Vancouver

Laboratoire d'Exploration Fonctionnelles, Nantes

Groupe Hospitalier Pitie-Salpetriere, Institut de Myologie, Paris

University of Essen - Clinic for Children, Essen

University Hospital, Freiburg im Breisgau

Hadassah University Hopspital, Jerusalem

Hospital Sant Joan de Deu, Barcelona

Hospital Universitario La Fe, Valencia

Astrid Lindgren Pediatric Hospital, Stockholm

UCL Instititute of Child Health, Dubowitz, London

University of Newcastle, Newcastle upon Tyne

Robert Jones & Agnes Hunt Orthopaedic Hospital, Oswestry

00165

Ospedale Pediatrico Bambino Gesu, Roma

00168

U.O. Complessa di Neuropsichiatria Infantile-Policlinico A. Gemelli-Universita Cattolica, Roma

S-416 85

Queen Silvia Children's Hospital, Gothenburg

Sponsors

Lead Sponsor

All Listed Sponsors
collaborator

Genzyme, a Sanofi Company

INDUSTRY

lead

PTC Therapeutics

INDUSTRY

NCT00847379 - Phase 2B Extension Study of Ataluren (PTC124) in Duchenne/Becker Muscular Dystrophy (DMD/BMD) | Biotech Hunter | Biotech Hunter