Study of Ataluren (PTC124™) in Cystic Fibrosis

PHASE3CompletedINTERVENTIONAL
Enrollment

238

Participants

Timeline

Start Date

September 8, 2009

Primary Completion Date

November 12, 2011

Study Completion Date

November 12, 2011

Conditions
Cystic Fibrosis
Interventions
DRUG

Ataluren

Ataluren will be provided as a vanilla-flavored powder to be mixed with water.

DRUG

Placebo

Placebo matching to ataluren will be provided.

Trial Locations (38)

10011

Beth Israel Medical Center, New York

10595

New York Medical College, Valhalla

15213

Childrens Hospital of Pittsburgh, Pittsburgh

21287

Johns Hopkins Children's Center, Baltimore

27599

University of North Carolina, Chapel Hill

30322

Emory University Cystic Fibrosis Center, Atlanta

31059

Hôpital des Enfants, Toulouse

33136

University of Miami, Miami

33155

Miami Children's Hospital, Miami

35233

University of Alabama-Birmingham, Birmingham

44106

Rainbow Babies & Children's Hospital, Cleveland

52242

University of Iowa, Iowa City

60614

Children's Memorial Hospital, Chicago

63110

Washington University, St Louis

75708

University of Texas, Tyler

80045

The Children's Hospital, Aurora

90806

Miller Children's Hospital Long Beach, Long Beach

91240

Hadassah University Hospital - Mount Scopus, Jerusalem

92123

Rady Children's Hospital - San Diego, San Diego

94304

Lucile Packard Children's Hospital, Palo Alto

Stanford, Palo Alto

98195

University of Washington, Seattle

02115

Children's Hospital Boston, Boston

Unknown

Hôpital Erasme, Brussels

Hôpital Universitaire des Enfants Reine Fabiola, Brussels

University Hospital Brussels, Brussels

University Hospital Leuven, Leuven

University of Toronto, Toronto

Hôpital Cochin, Paris

Hôpital Necker - Enfants Malades, Paris

Klinikum der Universität Köln, Cologne

Università La Sapienza, Rome

Azienda Ospedaliera di Verona, Verona

Universitair Medisch Centrum Utrecht, Utrecht

Hospital Universitario La Paz, Madrid

Karolinska University Hospital, Huddinge, Stockholm

Belfast City Hospital, Belfast

Alder Hey Children's Hospital, Liverpool

Sponsors

Lead Sponsor

All Listed Sponsors
collaborator

Cystic Fibrosis Foundation

OTHER

lead

PTC Therapeutics

INDUSTRY