45
Participants
Start Date
July 31, 2008
Primary Completion Date
May 31, 2018
Study Completion Date
May 31, 2018
Sapropterin (Kuvan)
20mg/kg/day taken once daily or as otherwise prescribed by physician as standard care.
Washington University, St Louis
Collaborators (1)
BioMarin Pharmaceutical
INDUSTRY
University of Missouri-Columbia
OTHER
Washington University School of Medicine
OTHER