PTC299 in Treating Patients With HIV-Related Kaposi Sarcoma

PHASE1/PHASE2TerminatedINTERVENTIONAL
Enrollment

17

Participants

Timeline

Start Date

September 30, 2008

Primary Completion Date

November 30, 2010

Study Completion Date

December 31, 2010

Conditions
Kaposi's Sarcoma
Interventions
DRUG

VEGF inhibitor PTC299

20 mg capsules to be taken by mouth BID. Three dose levels will be evaluated: 40 mg, 80mg, and 100mg BID. Subjects will receive PTC299 in consecutive 28-day cycles for a maximum of 12 cycles.

GENETIC

gene expression analysis

To describe the effects of PTC299 on viral gene expression and cellular gene transcription in KS tumor biopsies using real-time QPCR-based profiling.

GENETIC

polymerase chain reaction

To describe the effects of PTC299 on viral gene expression and cellular gene transcription in KS tumor biopsies using real-time QPCR-based profiling.

GENETIC

protein expression analysis

To describe the effects of PTC299 on viral gene expression and cellular gene transcription in KS tumor biopsies using real-time QPCR-based profiling.

OTHER

immunohistochemistry staining method

To describe the effects of PTC299 on KS tumor biopsies with respect to expression of VEGF, the VEGFR-2 and -3, phospho-Akt, p53, HIF-1α and proliferation, measured by Ki-67 staining.

OTHER

laboratory biomarker analysis

To describe the effects of PTC299 on KS tumor biopsies with respect to expression of VEGF, the VEGFR-2 and -3, phospho-Akt, p53, HIF-1α and proliferation, measured by Ki-67 staining.

OTHER

pharmacological study

To describe the pharmacokinetics of PTC299 in patients with HIV-associated KS. To describe the effects of PTC299 on circulating VEGF, VEGFR and cytokine levels in patients with HIV-associated KS.

PROCEDURE

biopsy

To describe the effects of PTC299 on KS tumor biopsies with respect to expression of VEGF, the VEGFR-2 and -3, phospho-Akt, p53, HIF-1α and proliferation, measured by Ki-67 staining.

Trial Locations (8)

10065

Memorial Sloan-Kettering Cancer Center, New York

96813

Cancer Research Center of Hawaii, Honolulu

98111

Floyd and Delores Jones Cancer Institute at Virginia Mason Medical Center, Seattle

92093-0658

Rebecca and John Moores UCSD Cancer Center, La Jolla

90033-1048

USC/Norris Comprehensive Cancer Center and Hospital, Los Angeles

90095-1793

UCLA Clinical AIDS Research and Education (CARE) Center, Los Angeles

02215

Beth Israel Deaconess Medical Center, Boston

43210-1240

Arthur G. James Cancer Hospital and Richard J. Solove Research Institute at Ohio State University Comprehensive Cancer Center, Columbus

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

National Cancer Institute (NCI)

NIH

collaborator

PTC Therapeutics

INDUSTRY

collaborator

The Emmes Company, LLC

INDUSTRY

lead

AIDS Malignancy Consortium

NETWORK

NCT00686842 - PTC299 in Treating Patients With HIV-Related Kaposi Sarcoma | Biotech Hunter | Biotech Hunter