40
Participants
Start Date
April 30, 2008
Primary Completion Date
May 31, 2012
Study Completion Date
June 30, 2012
Valproic Acid and Levocarnitine
Drug: Valproic Acid and Levocarnitine; syrup; dosage is by weight
Johns Hopkins University, Baltimore
Duke University Medical Center, Durham
Ohio State University Medical Center, Dept. of Neurology, Columbus
Children's Hospital of Michigan, Detroit
Klinikum der Universität zu Köln, Cologne
University of Utah/Primary Children's Medical Center, Salt Lake City
University of Wisconsin Children's Hospital, Madison
Hospital Sainte-Justine, Montreal
Collaborators (1)
Families of Spinal Muscular Atrophy
OTHER
Leadiant Biosciences, Inc.
INDUSTRY
University of Utah
OTHER