NCT00599781View on ClinicalTrials.gov

Gene Therapy for ADA-SCID

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

8

Participants

Timeline

Start Date

March 31, 1992

Primary Completion Date

July 31, 2006

Study Completion Date

January 31, 2007

Conditions
Severe Combined Immunodeficiency Syndrome
Interventions
GENETIC

gene transduced PBL and/or gene transduced HSC

infusions of autologous PBL and/or HSC transduced with retroviral vectors encoding ADA

All Listed Sponsors
collaborator

Fondazione Telethon

OTHER

lead

IRCCS San Raffaele

OTHER

NCT00599781 - Gene Therapy for ADA-SCID | Biotech Hunter | Biotech Hunter