NCT00515398View on ClinicalTrials.gov

A Study to Evaluate the Effects of Pharmacological Chaperones in Cells From Patients With Pompe Disease

CompletedOBSERVATIONAL
Enrollment

30

Participants

Timeline

Start Date

August 31, 2007

Primary Completion Date

January 31, 2008

Study Completion Date

January 31, 2008

Conditions
Pompe DiseaseGlycogen Storage Disease Type II
Interventions
OTHER

Observation

Ex vivo administration of AT2220

Trial Locations (4)

11042

Center for Metabolic Disorders, Lake Success

27708

Duke University, Durham

63110

Washington University, St Louis

32610-0296

University of Florida, Gainesville

Sponsors
All Listed Sponsors
lead

Amicus Therapeutics

INDUSTRY

NCT00515398 - A Study to Evaluate the Effects of Pharmacological Chaperones in Cells From Patients With Pompe Disease | Biotech Hunter | Biotech Hunter